New treatment for sickle cell disease

BestPractice | Jun 2019 | EHA 2019 |

Sickle cell disease is a genetic blood disorder that affects millions worldwide and can cause recurrent pain episodes and chronic anemia, leading to damaged organs, stroke and premature death. In this MEDtalk Jo Howard present data that show that voxelotor, a new treatment for sickle cell disease significantly improves anemia and hemolysis, and provides strong evidence that voxelotor has the potential to be a disease-modifying treatment that could prevent chronic organ damage.